Tipoffs on New England Newsletter for Monday May 05, 2025 ( 1 items ) |
University College London: Gene Therapy Offers Potential to Extend Lives of Children With Rare Immune Disorder
LONDON, England, May 4 -- The University College London issued the following news:
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Gene therapy offers potential to extend lives of children with rare immune disorder
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I, in an international clinical trial co-led by UCL.
The findings from the trials, which were led by researchers a
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