University College London: Gene Therapy Offers Potential to Extend Lives of Children With Rare Immune Disorder
May 04, 2025
May 04, 2025
LONDON, England, May 4 -- The University College London issued the following news:
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Gene therapy offers potential to extend lives of children with rare immune disorder
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I, in an international clinical trial co-led by UCL.
The findings . . .
* * *
Gene therapy offers potential to extend lives of children with rare immune disorder
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I, in an international clinical trial co-led by UCL.
The findings . . .