Findings point to path forward for treatment of rare genetic disease
December 10, 2025
December 10, 2025
CAMBRIDGE, Massachusetts, Dec. 10 [Category: Medical] -- The Broad Institute posted the following news:
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Findings point to path forward for treatment of rare genetic disease
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Friedreich's ataxia (FA) is a rare but devastating genetic disorder. Those with the condition are often diagnosed between 5 and 15 years of age and live only into their 30s or 40s. There is no widely approved treatment that modifies the disease, and existing the . . .
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Findings point to path forward for treatment of rare genetic disease
*
Friedreich's ataxia (FA) is a rare but devastating genetic disorder. Those with the condition are often diagnosed between 5 and 15 years of age and live only into their 30s or 40s. There is no widely approved treatment that modifies the disease, and existing the . . .