Personalized Gene Therapy Helps Teen with Rare Form of Severe Epilepsy Walk Independently
July 21, 2026
July 21, 2026
LA JOLLA, California, July 21 -- The University of California San Diego campus posted the following news:
* * *
Personalized Gene Therapy Helps Teen with Rare Form of Severe Epilepsy Walk Independently
*
Key Takeaways
* Investigational gene therapy with allele-selective antisense oligonucleotides silenced the expression of a mutant copy of the SCN2A gene, dramatically reducing seizure frequency.
* Broad developmen . . .
* * *
Personalized Gene Therapy Helps Teen with Rare Form of Severe Epilepsy Walk Independently
*
Key Takeaways
* Investigational gene therapy with allele-selective antisense oligonucleotides silenced the expression of a mutant copy of the SCN2A gene, dramatically reducing seizure frequency.
* Broad developmen . . .