UCLA Scientists Advance Gene Therapy for Deadly Blood Disorder
September 18, 2025
September 18, 2025
LOS ANGELES, California, Sept. 18 -- The University of California issued the following news release:
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UCLA scientists advance gene therapy for deadly blood disorder
The technology renewed the ability of cells of patients with alpha thalassemia major to produce hemoglobin
Key takeaways
* UCLA researchers have made strides in developing a stem cell gene therapy for alpha thalassemia major, a severe, inherited blood disorder in w . . .
* * *
UCLA scientists advance gene therapy for deadly blood disorder
The technology renewed the ability of cells of patients with alpha thalassemia major to produce hemoglobin
Key takeaways
* UCLA researchers have made strides in developing a stem cell gene therapy for alpha thalassemia major, a severe, inherited blood disorder in w . . .