Customized Gene-Editing Technology Shows Potential to Treat Lethal Pediatric Disease
September 11, 2025
September 11, 2025
BOSTON, Massachusetts, Sept. 11 [Category: BizHospital] -- Mass General Brigham issued the following news release:
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Customized Gene-Editing Technology Shows Potential to Treat Lethal Pediatric Disease
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Multisystemic smooth muscle dysfunction syndrome (MSMDS) is a rare condition associated with stroke, aortic dissection (tearing) and death in childhood. Currently, there is no effective treatment or cure for MSMDS. A single error in the gen . . .
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Customized Gene-Editing Technology Shows Potential to Treat Lethal Pediatric Disease
*
Multisystemic smooth muscle dysfunction syndrome (MSMDS) is a rare condition associated with stroke, aortic dissection (tearing) and death in childhood. Currently, there is no effective treatment or cure for MSMDS. A single error in the gen . . .