FDA Grants Orphan Drug Designation to UAB-developed Gene Therapy for ALS
July 16, 2025
July 16, 2025
BARCELONA, Spain, July 16 -- The Autonomous University of Barcelona issued the following news:
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FDA grants orphan drug designation to UAB-developed gene therapy for ALS
The treatment, licensed to Klotho Neurosciences, is based on a technology developed at the Universitat Autonoma de Barcelona (UAB).
The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to a new gene therapy for Amyotrophic Lateral Sclerosis (ALS) . . .
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FDA grants orphan drug designation to UAB-developed gene therapy for ALS
The treatment, licensed to Klotho Neurosciences, is based on a technology developed at the Universitat Autonoma de Barcelona (UAB).
The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to a new gene therapy for Amyotrophic Lateral Sclerosis (ALS) . . .