Kennedy Krieger Researcher Helps Advance Potential Drug for Fatal Childhood Brain Disease
May 30, 2025
May 30, 2025
BALTIMORE, Maryland, May 30 -- Kennedy Krieger Institute issued the following news release:
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Kennedy Krieger Researcher Helps Advance Potential Drug for Fatal Childhood Brain Disease
A Kennedy Krieger Institute researcher is playing a role in a major international effort that has yielded a promising first-ever drug treatment for cerebral adrenoleukodystrophy (cALD)--a rare, often fatal genetic brain disease that impacts boys between ages 3 and 12.
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Kennedy Krieger Researcher Helps Advance Potential Drug for Fatal Childhood Brain Disease
A Kennedy Krieger Institute researcher is playing a role in a major international effort that has yielded a promising first-ever drug treatment for cerebral adrenoleukodystrophy (cALD)--a rare, often fatal genetic brain disease that impacts boys between ages 3 and 12.