Gene Therapy Restores Immune Function and Extends Lives of Children With Rare Immune Disorder
May 01, 2025
May 01, 2025
LOS ANGELES, California, May 1 -- The UCLA Health issued the following news release:
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Gene therapy restores immune function and extends lives of children with rare immune disorder
9 children born with severe LAD-l are symptom-free two years after treatment
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion . . .
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Gene therapy restores immune function and extends lives of children with rare immune disorder
9 children born with severe LAD-l are symptom-free two years after treatment
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion . . .