Autonomous University of Barcelona: Gene Therapy Reverses Symptoms of Rare Neurological Disease in Animal Models
April 01, 2025
April 01, 2025
BARCELONA, Spain, April 1 -- The Autonomous University of Barcelona issued the following news:
* * *
Gene therapy reverses symptoms of rare neurological disease in animal models
A recent study led by the UAB demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, Megalencephalic Leukoencephalopathy with Subcortical Cysts (MLC), even when treatment begins after symptom onset.
MLC is a rare childhood neurolo . . .
* * *
Gene therapy reverses symptoms of rare neurological disease in animal models
A recent study led by the UAB demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, Megalencephalic Leukoencephalopathy with Subcortical Cysts (MLC), even when treatment begins after symptom onset.
MLC is a rare childhood neurolo . . .