Repurposed Drug May Help Stabilize Vision in Rare Disease
June 18, 2024
June 18, 2024
ST. LOUIS, Missouri, June 18 (TNSres) -- The Washington University St. Louis School of Medicine issued the following news release:
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Clinical trial for RVCL-S patients tests drug already approved as sickle cell disease treatment
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Roughly 50 families scattered across the world share ultra-rare variants in a particular gene. Silent for years, the inherited mutations make themselves known when patients reach the fourth decade of life. Cha . . .
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Clinical trial for RVCL-S patients tests drug already approved as sickle cell disease treatment
* * *
Roughly 50 families scattered across the world share ultra-rare variants in a particular gene. Silent for years, the inherited mutations make themselves known when patients reach the fourth decade of life. Cha . . .