Experimental Gene Therapy for Giant Axonal Neuropathy Shows Promise in NIH Clinical Trial
March 21, 2024
March 21, 2024
WASHINGTON, March 21 (TNSres) -- The U.S. Department of Health and Human Services' National Institutes of Health issued the following news release on March 20, 2024:
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Treatment for rare childhood disease was well tolerated and slowed loss of motor function.
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An investigational gene therapy for a rare neurodegenerative disease that begins in early childhood, known as giant axonal neuropathy (GAN), was well tolerated and showed signs of . . .
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Treatment for rare childhood disease was well tolerated and slowed loss of motor function.
* * *
An investigational gene therapy for a rare neurodegenerative disease that begins in early childhood, known as giant axonal neuropathy (GAN), was well tolerated and showed signs of . . .