Duke Experts Participate in First Use of Fetal Therapy for Pompe Disease
November 10, 2022
November 10, 2022
DURHAM, North Carolina, Nov. 10 (TNSres) -- Duke Health issued the following news release:
Experts at Duke Health were among a multi-national team involved in treating a fetus for infantile-onset Pompe disease using an enzyme replacement therapy - a first in the world.
The case, reported online Nov. 9 in the New England Journal of Medicine, highlights the potential for introducing a therapy for Pompe disease prior to birth. Even in the womb, the lysosomal storage diseas . . .
Experts at Duke Health were among a multi-national team involved in treating a fetus for infantile-onset Pompe disease using an enzyme replacement therapy - a first in the world.
The case, reported online Nov. 9 in the New England Journal of Medicine, highlights the potential for introducing a therapy for Pompe disease prior to birth. Even in the womb, the lysosomal storage diseas . . .