Wednesday - August 5, 2026
Children's Hospital of Philadelphia: Existing Class of Drugs May Improve Neurological Function in Patients With Rare, Aggressive Genetic Disorder
September 11, 2020
PHILADELPHIA, Pennsylvania, Sept. 11 (TNSRes) -- Children's Hospital of Philadelphia issued the following news:

New findings from Children's Hospital of Philadelphia (CHOP) show that some patients with a rare and aggressive form of leukodystrophy may benefit from receiving treatment with a class of targeted therapy drugs that could improve their neurological function. A correspondence about these findings was published in the New England Journal of Medicine.

A . . .

Targeted News Service Document Request Form

This document is available to you by e-mail if you complete the form below with relevant information. There may be a fee for this article or ongoing service of similar materials. We will be in touch shortly.

Click here for more information about our products