Yeshiva University: Drug Target for Rare Disease
May 02, 2020
May 02, 2020
BRONX, New York, May 2 -- Yeshiva University's Albert Einstein College of Medicine issued the following news release:
Adult-onset leukoencephalopathy with axonal spheroids and pigmented glia (ALSP) is a rare, dominantly inherited, neurodegenerative disorder caused by mutations in the receptor (CSF-1R) for the growth factor CSF-1. There are no available treatments for ALSP patients, who generally die within 5 to 7 years of the appearance of disease symptoms.
In a study o . . .
Adult-onset leukoencephalopathy with axonal spheroids and pigmented glia (ALSP) is a rare, dominantly inherited, neurodegenerative disorder caused by mutations in the receptor (CSF-1R) for the growth factor CSF-1. There are no available treatments for ALSP patients, who generally die within 5 to 7 years of the appearance of disease symptoms.
In a study o . . .