ICYMI: MATSUI, BILIRAKIS INTRODUCE LEGISLATION TO GIVE SCIENTISTS ENHANCED FORMAL ROLE IN DEVELOPMENT OF RARE DISEASE TREATMENTS
November 12, 2024
November 12, 2024
WASHINGTON, Nov. 12 -- Rep. Doris O. Matsui, D-California, issued the following news release:
CongresswomanDoris Matsui (D-CA-07)and Congressman Gus Bilirakis (R-FL-12), co-chairs of the Rare Disease Congressional Caucus, introduced the Scientific External Process for Educated Review of Therapeutics (EXPERT) Act of 2024, legislation to formalize the Externally-Led Scientific-Focused Drug Development (EL-SFDD) meeting at FDA.
Over 90% of rare diseases have no FDA-approv . . .
CongresswomanDoris Matsui (D-CA-07)and Congressman Gus Bilirakis (R-FL-12), co-chairs of the Rare Disease Congressional Caucus, introduced the Scientific External Process for Educated Review of Therapeutics (EXPERT) Act of 2024, legislation to formalize the Externally-Led Scientific-Focused Drug Development (EL-SFDD) meeting at FDA.
Over 90% of rare diseases have no FDA-approv . . .