Perelman School of Medicine: Advances Recognized in Treatment of Rare Diseases
May 25, 2019
May 25, 2019
PHILADELPHIA, Pennsylvania, May 25 [TNSresearch] -- The University of Pennsylvania's Perelman School of Medicine issued the following news release:
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- Newly Approved Spinal Muscle Atrophy Treatment Zolgensma Is Based on Delivery System Discovered By Penn Gene Therapy Pioneer
- Approval Marks a New Milestone in Quest to Treat Rare Diseases
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James Wilson, MD, PhD, recalls being struck by the devastating toll of rare disease . . .
* * *
- Newly Approved Spinal Muscle Atrophy Treatment Zolgensma Is Based on Delivery System Discovered By Penn Gene Therapy Pioneer
- Approval Marks a New Milestone in Quest to Treat Rare Diseases
* * *
James Wilson, MD, PhD, recalls being struck by the devastating toll of rare disease . . .